Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
Thalassaemia - The Lancet
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
A systematic review of quality of life in sickle cell disease and thalassemia after stem cell transplant or gene therapy - ScienceDirect
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon | Article
Β-Thalassemias | NEJM
Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
PDF) Cure for thalassemia major – From allogeneic hematopoietic stem cell transplantation to gene therapy
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
IJMS | Free Full-Text | Iron Overload and Chelation Therapy in Non-Transfusion Dependent Thalassemia
Gene therapies for transfusion dependent β‐thalassemia: Current status and critical criteria for success - Soni - 2020 - American Journal of Hematology - Wiley Online Library
Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica
Cureus | Blood Demand and Challenges for Patients With Beta-Thalassemia Major in Eastern Saudi Arabia | Article
Plasma proteome profiling combined with clinical and genetic features reveals the pathophysiological characteristics of β-thalassemia - ScienceDirect
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Guidelines for the Management of Non-Transfusion Dependent Thalassaemias (2nd edition - 2017) by Thalassaemia International Federation (TIF) - Issuu
Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu
Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review
